Spark Therapeutics is a fully integrated, commercial company committed to discovering, developing and delivering gene therapies. Spark Therapeutics has a product portfolio addressing inherited retinal diseases (IRDs), liver-directed diseases, and neurodegenerative diseases. The Company's validated platform for gene therapy vector design and manufacturing has enabled it to become a leader in the field of gene therapy. Spark Therapeutics' mission is to challenge the inevitability of genetic disease by discovering, developing, and delivering treatments in ways unimaginable - until now.